BioSpace

Cure Rare Disease Awarded $7.4 Million CIRM Grant to Advance Gene Therapy for Limb-Girdle Muscular Dystrophy Type 2i/R9

WOODBRIDGE, Conn.--(BUSINESS WIRE)--Cure Rare Disease (CRD) announced it has been awarded a $7.4 million grant from the California Institute for Regenerative Medicine (CIRM) to advance the development ...
Morningstar

Cure Rare Disease Awarded $7.4 Million CIRM Grant to Advance Gene Therapy for Limb-Girdle Muscular Dystrophy Type 2i/R9

Cure Rare Disease (CRD) announced it has been awarded a $7.4 million grant from the California Institute for Regenerative Medicine (CIRM) to advance the development of a novel gene therapy for ...
Mashable

What is gait analysis? And can this forensics tool positively identify a suspect?

Gait analysis is often used in sports medicine, as seen in this picture. Credit: Daniel Karmann/picture alliance via Getty Images Over the weekend, the conservative media outlet The Blaze and ...
The Business Journals

BridgeBio's stock soars after stunning early data against a deadly rare disease

To continue reading this content, please enable JavaScript in your browser settings and refresh this page. Preview this article 1 min The search for a treatment for ...
Seeking Alpha

BridgeBio Pharma, Inc. (BBIO) Discusses Positive FORTIFY Phase III Interim Results in Limb-Girdle Muscular Dystrophy Type 2I/R9 Transcript

Ladies and gentlemen, thank you for standing by. My name is Krista, and I will be your conference operator today. At this time, I would like to welcome everyone to the BridgeBio Pharma Limb-Girdle ...
BioWorld

‘Home run scenario’ for Bridgebio’s BBP-418 in limb-girdle phase III

Impressive data from an interim readout of Bridgebio Pharma Inc.’s BBP-418 in limb-girdle muscular dystrophy type 2I/R9 has the company prepping to meet with the U.S. FDA to discuss plans for the ...
STAT

BridgeBio study data on drug for rare form of muscular dystrophy could set up approval

Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...
STAT

Sarepta to seek approval for gene therapy in rare form of muscular dystrophy

Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...
Business Wire

Cure Rare Disease Secures FDA Orphan Drug Designation for Investigational Gene Therapy to Treat Limb-Girdle Muscular Dystrophy Type R9 (LGMD2i/R9)

WOODBRIDGE, Conn.--(BUSINESS WIRE)--Cure Rare Disease (CRD), a 501(c)(3) nonprofit biotechnology company developing genetic therapies for ultra-rare neuromuscular diseases, today announced that the ...
Science News

The brain preserves maps of missing hands for years

The brain holds space for a missing limb, even years after it’s gone. For three women who underwent planned hand amputations, brain scans revealed remarkably durable maps of hand areas, lasting for ...
Women's Health

Scientists Think They've Found A New Way To Help Aching Joints—Without Surgery Or Medications

If you’re dealing with knee pain that just won’t quit, you could have something called osteoarthritis, a painful disease where the cartilage that cushions your joints is worn down. While treatments ...
Scientific American

The Brain’s Map of the Body Is Surprisingly Stable—Even after a Limb Is Lost

A brain-imaging study of people with amputated arms has upended a long-standing belief: that the brain’s map of the body reorganizes itself to compensate for missing body parts. Previous research had ...